Gene therapy for rare diseases involves the introduction of genetic material into a patient's cells to treat or prevent a rare genetic disorder. It offers great potential in addressing diseases that have no cure or limited treatment options. This therapy holds immense advantages, including the potential to provide long-term solutions, target specific genetic mutations, and improve patient outcomes and quality of life. The increasing incidence of rare diseases ... Read more
Gene therapy is an experimental technique that uses genes to treat or prevent disease. In rare diseases, gene therapy aims to supplement a missing gene or inactivate a faulty gene that is causing disease. Diseases like hemophilia, cystic fibrosis, sickle cell anemia, and several types of blindness and cancer are potential targets for gene therapy. The global rare disease treatment market is largely driven by rising investment in research and development for orphan drugs and gene therapies. ... Read more
Gene therapy is an experimental technique that uses genes to treat or prevent disease. In rare diseases, gene therapy aims to supplement a missing gene or inactivate a faulty gene that is causing disease. Diseases like hemophilia, cystic fibrosis, sickle cell anemia, and several types of blindness and cancer are potential targets for gene therapy. The global rare disease treatment market is largely driven by rising investment in research and development for orphan drugs and gene therapies. ... Read more
