The global gene therapy for rare disease market size was valued at US$ 16.3 million in 2017, and is expected to witness a robust CAGR of 35.0% over the forecast period (2018–2026).
In recent past, key players in the market have gained regulatory approvals and have launched their therapies in the market. Frequent approvals of novel gene therapies and their launches in the developed regions are expected to significantly drive gene therapy for rare disease market growth over the ... Read more
Gene therapy involves insertion of genetic material into cells of the patients to provide new function or to restore missing or inappropriate functioning of the cells due to cancer or gene mutations. According to National Center for Advancing Translational Sciences, although around 7,000 rare diseases are identified, only a few hundred have approved treatments. Moreover, developing gene therapy for rare diseases is ... Read more
Gene therapy for rare diseases involves the introduction of genetic material into a patient's cells to treat or prevent a rare genetic disorder. It offers great potential in addressing diseases that have no cure or limited treatment options. This therapy holds immense advantages, including the potential to provide long-term solutions, target specific genetic mutations, and improve patient outcomes and quality of life. The increasing incidence of rare diseases ... Read more
The Gene Therapy For Rare Disease Market is estimated to be valued at US$ 193.56 Bn in 2023 and is expected to exhibit a CAGR of 11.% over the forecast period 2023 to 2030, as highlighted in a new report published by Coherent Market Insights.
Market Overview:
Gene therapy for rare diseases uses genetic material to treat or cure diseases caused by errors in genes or chromosomes.It involves inserting a functional ... Read more
Gene therapy for rare disease involves gene transfer techniques that alter or modify the expression of a gene or its activity to cure genetic disorders. Gene therapy is emerging as a viable treatment option for various rare genetic diseases, such as hemophilia, hearing loss, retinitis pigmentosa, Gaucher's disease, and Sanfilippo syndrome, for which conventional treatment options are not available or are highly inadequate. The method is advantageous as it can potentially provide a functional ... Read more
Gene therapy is an experimental technique that uses genes to treat or prevent disease. In rare diseases, gene therapy aims to supplement a missing gene or inactivate a faulty gene that is causing disease. Diseases like hemophilia, cystic fibrosis, sickle cell anemia, and several types of blindness and cancer are potential targets for gene therapy. The global rare disease treatment market is largely driven by rising investment in research and development for orphan drugs and gene therapies. ... Read more
Gene therapy is an experimental technique that uses genes to treat or prevent disease. In rare diseases, gene therapy aims to supplement a missing gene or inactivate a faulty gene that is causing disease. Diseases like hemophilia, cystic fibrosis, sickle cell anemia, and several types of blindness and cancer are potential targets for gene therapy. The global rare disease treatment market is largely driven by rising investment in research and development for orphan drugs and gene therapies. ... Read more
